Working toward a Cure
FRAXA's mission is to find effective treatments and a cure for all children and adults with Fragile X, by directly funding the most promising research. As the pace of Fragile X research accelerates, the prospects of finding effective treatments and a cure for Fragile X and autism continue to improve. FRAXA-funded researchers at universities around the world are leading the way.
FRAXA's research portfolio spans the spectrum of basic science, pre-clinical, and clinical research -- all coordinated to make the most of each dollar. We maintain a diversified approach, developing several treatment strategies in parallel, since success is never certain in developing a single drug. We continue to fund research to define the precise defect in the Fragile X brain, because these basic studies may yield additional important therapeutic targets.
Where are we now?
In the words of FRAXA Scientific Advisor Dr. Justin Fallon, "Fragile X is poised to become a triumph for translational research and the design of rational therapeutics for brain disease."
>Summary of Findings: What do we know and how close are we to a cure?
>Treatment Trials: Here you will find a listing of trials and studies currently accepting participants with Fragile X.
>Research Reports: Review all FRAXA grants here. Each FRAXA investigator has a page about his/her work.
>Applying for FRAXA Grants: Research priorities, application information, renewal and final report guidelines.
>Research Meetings: FRAXA organizes and sponsors conferences where scientists share discoveries, plan collaborations, and bring new researchers into the field. FRAXA Investigators Meetings run every 2 years (2013, 2015, etc.) and Gordon Conferences on Fragile X and Autism run alternate years.
>Research Resources: mutant mouse resource, reagents including experimental compounds, antibodies, mice, and tissue.